Scientific American - USA (2020-03)

46 Scientific American, March 2020

Photographs by Ethan Hill

Finally

Making

Sense

A long-disdained therapy that targets RNA

is achieving spectacular success

By Lydia Denworth

ANTISENSE THERAPY

ONE OF THE FIRST children

ever to benefit from an anti-

sense drug, Emma Larson, at

her home in Long Island, N.Y.

© 2020 Scientific American © 2020 Scientific American